CRISPR technology for the treatment of deafness with genetic causes

The journal Nature has published an article reporting a new, significant success of CRISPR technology–Cas9. A team of researchers led by David R. Liu, at Rice University of Houston has succeeded in correcting, using CRISPR technology, a mutant form of the gene Tmc1, responsible for a type of genetic deafness. The experiment has been conducted by encapsulating CRISPR components in positively charged fatty molecules, which are capable of crossing cell membranes. Once inside the cell, the CRISPR–Cas9 enzyme corrects the gene’s DNA. Up to now, the experiment has been conducted exclusively on laboratory mice, and several more experiments and years will be necessary before this approach can be tested on humans.

(Source: Nature)