Rare diseases: latest news - GoINPHARMA
Sunday, 23 September 2018 - 5:52

Rare diseases

Rare diseases: FDA awards grants over 6 million dollars

FDA has announced it has awarded six grants for rare diseases research. Specifically, the studies will focus on rare disease natural history, that is the course a disease takes from its onset, through the presymptomatic and clinical stages, to a…

The market of rare disease drugs

Rare diseases are surely among the most interesting therapeutic areas for the pharmaceutical industry, and they have been since the 1990s, when US-based Genzyme proposed a treatment for Gaucher’s disease at up to $300,000. According to a recent report by…